See how a childhood friendship inspired and motivated a researcher to dedicate his career to finding a cure for muscular dystrophy.
Michael Lawlor, MD, PhD, assistant professor of pathology and director of the pediatric pathology neuromuscular laboratory at the Medical College of Wisconsin, is involved in a worldwide collaboration to develop a cure for X-linked myotubular myopathy (XLMTM), a severe rare disease characterized by profound muscle weakness, respiratory failure and early death. Over the last five years, the team has uncovered a gene therapy for XLMTM that shows great clinical potential. Modern research advancements like this are giving renewed hope to families like the Whistons who previously had none.
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